TY  - JOUR

T1  - Rationale, design, and methods of a randomized, controlled, open-label clinical trial with open-label extension to investigate the safety of vosoritide in infants, and young children with achondroplasia at risk of requiring cervicomedullary decompression surgery

JO  - Science Progress

PY  - 2021/03/25

AU  - Savarirayan R

AU  - Irving M

AU  - Maixner W

AU  - Thompson D

AU  - Offiah AC

AU  - Connolly DJA

AU  - Raghavan A

AU  - Powell J

AU  - Kronhardt M

AU  - Jeha G

AU  - Ghani S et al

ED  - 

DO  - DOI: 10.1177/00368504211003782

PB  - SAGE Publications

VL  - 104

IS  - 1

Y2  - 2024/12/27

ER  -