@article{article, title = {{Safety, tolerability, and pharmacokinetics of antisense oligonucleotide BIIB078 in adults with C9orf72-associated amyotrophic lateral sclerosis: a phase 1, randomised, double blinded, placebo-controlled, multiple ascending dose study}}, publisher = {{Elsevier BV}}, url = {{http://dx.doi.org/10.1016/s1474-4422(24)00216-3 }}, year = {{2024}}, month = {{7}}, author = {{van den Berg LH and Rothstein JD and Shaw PJ and Babu S and Benatar M and Bucelli RC and Genge A and Glass JD and Hardiman O and Libri V and Mobach T et al}}, doi = {{10.1016/s1474-4422(24)00216-3}}, journal = {{The Lancet Neurology}}, note = {{Accessed on 2024/12/26}}}