TY - JOUR T1 - Systemic restoration of UBA1 ameliorates disease in spinal muscular atrophy JO - JCI Insight UR - http://eprints.whiterose.ac.uk/102790/ PY - 2016/07/21 AU - Azzouz M ED - DO - DOI: 10.1172/jci.insight.87908 VL - 1 IS - 11 Y2 - 2024/12/25 ER -